A Santa Cruz family received a fully adaptable van for their 12-year-old son with Duchenne muscular dystrophy, funded by ...
Data underscore the differentiated capability of the clinically validated FORCE platform to cross the blood-brain barrier - ...
Gillette Children’s Specialty Healthcare in St. Paul was first to set up special program for providing still-experimental ...
Santhera Pharmaceuticals (SIX:SANN, OTC:SPHDF, FRA:S3F0), the Swiss rare disease specialist, has received a positive opinion ...
The EMA has backed broader pediatric use of Agamree and Crysvita, lowering age thresholds for rare genetic diseases affecting muscle and bone development.
Santhera Pharmaceuticals (SIX: SANN) today announced that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion recommending ...
An Oxfordshire barrister living with muscular dystrophy has been named Campaigner of the Year by the national charity ...
A Morris dancer from Hastings is hoping to break a world record when he runs Sunday's London Marathon - and he said he was ...
A disabled Twitch streamer known for beating difficult games with his chin has returned to the platform to beat Super Mario ...
Deramiocel is a novel cellular therapy that demonstrated benefit on skeletal muscle function in the HOPE-2 phase II study of ...
The FDA is signaling change, but actual success depends on more than simply bringing in a new leader at the Center for ...
Scientists sum up the evidence—or lack thereof—for the most popular peptides hyped for athletic performance and recovery.