SOLVE FSHD Announces Recent Grant Awards to Accelerate Treatments for Facioscapulohumeral Muscular Dystrophy

SOLVE FSHD, a venture philanthropy organization dedicated to accelerating treatments for facioscapulohumeral muscular ...

Santhera Receives Positive CHMP Opinion to Expand AGAMREE® (vamorolone) Use in Pediatric DMD Patients Aged Two and Older in the EU

Santhera Pharmaceuticals (SIX: SANN) today announced that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion recommending ...
Medscape

EMA Pushes Earlier Intervention in Rare Pediatric Diseases

The EMA has backed broader pediatric use of Agamree and Crysvita, lowering age thresholds for rare genetic diseases affecting muscle and bone development.
MedPage Today on MSN

Cell Therapy Slows Upper Limb Decline in Duchenne Muscular Dystrophy

Investigational deramiocel is back under FDA review again ...

Santhera wins backing to extend DMD drug AGAMREE to toddlers as young as two

Santhera Pharmaceuticals (SIX:SANN, OTC:SPHDF, FRA:S3F0), the Swiss rare disease specialist, has received a positive opinion ...

Santa Cruz community raises $97,000 for adaptive van for boy with Duchenne muscular dystrophy

A Santa Cruz family received a fully adaptable van for their 12-year-old son with Duchenne muscular dystrophy, funded by ...
Everyday Health on MSN

What kind of exercise is safe when you have Duchenne muscular dystrophy?

Learn how to exercise safely with Duchenne muscular dystrophy, for your flexibility, mobility, and overall health, without ...

Alan Osmond Did Not 'Fear the Future' After MS Diagnosis, Thanks to His Mormon Faith and the Support of His Family

Osmond enjoyed the support of his siblings and his own children as he reconfigured his life ...

Retailers Nationwide Partner with Muscular Dystrophy Association to Send Hundreds of Young People to Life-Changing Summer Camp

More than 1,000 stores support pinup and roundup campaigns to help kids and young adults living with neuromuscular diseases ...
Medscape

Therapy Insight: Cardiovascular Complications Associated With Muscular Dystrophy

The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...